Gene Therapy-MKGIMI BIOTECH

Gene Therapy

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Trial title

Estimated Enrollment

Partner

NCT03961243 Lentiviral FIX Gene Therapy for Hemophilia B'

Estimated Enrollment:
10
NCT03727555 Lentiviral Gene Therapy for X-linked Adrenoleukodystrophy (X-ALD)'

Estimated Enrollment:
10
NCT03725670 Gene Therapy for Metachromatic Leukodystrophy (MLD) Using a Self-inactivating Lentiviral Vector (TYF-ARSA)'

Estimated Enrollment:
10
NCT03645486 Lentiviral Gene Therapy for Chronic Granulomatous Disease (CGD)'

Estimated Enrollment:
10
NCT03645460 Gene Transfer for Adenosine Deaminase-severe Combined Immunodeficiency (ADA-SCID) Using an Improved Self-inactivating Lentiviral Vector (TYF-ADA)'

Estimated Enrollment:
10
NCT03351868 FANC-A Gene Transfer for Fanconi Anemia Using a Self-inactivating Lentiviral Vector'

Estimated Enrollment:
10
NCT03217617 Gene Therapy for X-linked Severe Combined Immunodeficiency (SCID-X1) Using a Self Lentiviral Vector'

Estimated Enrollment:
10
NCT03159364 Phase I/II Multicenter Trial of Antigen-specific Cytotoxic T Cells in the Treatment of Opportunistic Infections'

Estimated Enrollment:
100
NCT03351829 Gene Therapy of Beta Thalathemia Using a Self-inactivating Lentiviral Vector'

Estimated Enrollment:
20
NCT03217032 Lentiviral FVIII Gene Therapy for Hemophilia A'

Estimated Enrollment:
10